Groundbreaking Results from Avidity's FORTITUDE™ Trial Display Exceptional Progress in Gene Reduction and Functional Enhancement
Wednesday, 12 June 2024, 08:28
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Exciting Outcomes Unveiled
Avidity's AOC 1020 data from the Phase 1/2 FORTITUDE™ Trial exhibit a groundbreaking development - a notable decrease surpassing 50% in DUX4 regulated genes.
Positive Functional Indicators
The trial also reveals promising trends towards functional improvement, implying a potential paradigm shift in addressing gene-related challenges.
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